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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
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Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Dystrophine
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Homeostasis
Duchenne DMD dystrophy
Cell Line
Skeletal muscle
Dynamin 2
Calcium Channels
Genomic
Allele‐specific silencing therapy
Mdx mouse
Modificateurs de gènes
Delivery
Cells
Humans
Cell Biology
Muscles/physiopathology
Inbred mdx
Dystrophin central domain
CaV subunits
Metabolism
Energy Metabolism/drug effects
Muscle
Muscular dystrophy
Mitochondrial fission
Multi exon skipping
Muscle Strength
Base Sequence
Cultured
Clinical trials
Knockout
Génomique
Exon skipping
Dystrophie musculaire de Becker
Antisense oligonucleotides
LKB1
Diseases
MES
Becker BMD muscular dystrophy
Myogenesis
MiARN
CTNNB1
L-Type
Dystrophin
Duchenne muscular dystrophy
Centronuclear myopathy
Inbred C57BL
Dystrophy
Male
Activin Receptors
Multiresolution modeling
Animal/physiopathology
Hepatocellular carcinoma
Inhibitors
Multi resolution modeling
NAD+
Muscle development
Calcium
Myotendinous junction
Cardiomyopathy
DMO
Long QT
Liver
Becker muscular dystrophy BMD
Dystrophin-EGFP
Human Umbilical Vein Endothelial Cells
Animals
Gene expression
LncRNA
Becker muscular dystrophy
Long noncoding RNA
Duchenne muscular dystrophy DMD
Gene Expression Regulation/drug effects
Invivo
CD38
CaVβs
Dystrophie Musculaire de Duchenne DMD
Ex-vivo
Immunoglobulin Fc Fragments/pharmacology
Muscular Atrophy
Drp1
NNOS
Dystrophie Musculaire de Becker BMD
Cachexia
Molecular Sequence Data
Cell homeostasis
BMD
Gene modifiers
LncARN
Hear
Muscle Biology
Cardiomyopathie
Autophagy
Molecular docking
Mice
DMD
Epigenetics
DHPR α1S
Muscular Dystrophy
Morphogenesis